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All-RNA-mediated targeted gene integration in mammalian cells with rationally engineered R2 retrotransposons 期刊论文
CELL, 2024, 卷号: 187, 期号: 17
作者:  Chen, Yangcan;  Luo, Shengqiu;  Hu, Yanping;  Mao, Bangwei;  Wang, Xinge;  Lu, Zongbao;  Shan, Qingtong;  Zhang, Jin;  Wang, Siqi;  Feng, Guihai;  Wang, Chenxin;  Liang, Chen;  Tang, Na;  Niu, Rui;  Wang, Jiaqiang;  Han, Jiabao;  Yang, Ning;  Wang, Haoyi;  Zhou, Qi;  Li, Wei
Adobe PDF(6880Kb)  |  收藏  |  浏览/下载:3/0  |  提交时间:2025/11/06
REVERSE-TRANSCRIPTASE  LENTIVIRUS VECTORS  READ ALIGNMENT  MESSENGER-RNA  DNA  PROTEIN  SEQUENCE  INITIATION  CLEAVAGE  THERAPY  
Self-Assembled R848/Chlorin e6 Nanoparticles for Combinatorial Immunotherapy of Head and Neck Squamous Cell Carcinoma 期刊论文
ACS APPLIED NANO MATERIALS, 2024, 卷号: 7, 期号: 7, 页码: 7966-7977
作者:  Hu, Houyang;  Wang, Xuechun;  Zhao, Yilei;  Yan, Jie;  Li, Songyan;  Li, Chengzhilin;  Zhao, Xiaonan;  Sekhar, Kanaparedu P. C.;  Xia, Ming;  Jiao, Jianwei;  Zhao, Miaoqing;  Zhang, Guiqiang
收藏  |  浏览/下载:5/0  |  提交时间:2025/11/06
THERAPY  
Knockout and Replacement Gene Surgery to Treat Rhodopsin-Mediated Autosomal Dominant Retinitis Pigmentosa 期刊论文
HUMAN GENE THERAPY, 2024, 卷号: 35, 期号: 5-6, 页码: 151-162
作者:  Sun, Xuehan;  Liang, Chen;  Chen, Yangcan;  Cui, Tongtong;  Han, Jiabao;  Dai, Moyu;  Zhang, Ying;  Zhou, Qi;  Li, Wei
Adobe PDF(1262Kb)  |  收藏  |  浏览/下载:6/2  |  提交时间:2025/11/06
RETINAL FUNCTION  TRANSGENIC MICE  MUTATION  GENERATION  THERAPY  ALLELE  MODEL  STEP  RAT  
One-step cell biomanufacturing platform: porous gelatin microcarrier beads promote human embryonic stem cell-derived midbrain dopaminergic progenitor cell differentiation in vitro and survival after transplantation in vivo 期刊论文
NEURAL REGENERATION RESEARCH, 2024, 卷号: 19, 期号: 2, 页码: 458-464
作者:  Feng, Lin;  Li, Da;  Tian, Yao;  Zhao, Chengshun;  Sun, Yun;  Kou, Xiaolong;  Wu, Jun;  Wang, Liu;  Gu, Qi;  Li, Wei;  Hao, Jie;  Hu, Baoyang;  Wang, Yukai
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PRECLINICAL EFFICACY  NEURAL PROGENITORS  NEURONS  MODEL  BRAIN  GENERATION  INHIBITION  MATURATION  APOPTOSIS  THERAPY